Rare Disease Research Funding
A curated list of funding opportunities for rare disease research worldwide - the disease may be rare but the funding does not have to be.
Junior Investigator Global ATTR Amyloidosis Research ASPIRE
The Junior Investigator Global ATTR Amyloidosis Research ASPIRE from Pfizer supports early-career principal investigators worldwide (except for the USA) working on ATTR Amyloidosis. The grant seeks to fund projects on:
Clinical Fellowship – 3rd and 4th year (cystic fibrosis USA)
The 3rd and 4th year Clinical Fellowship from the Cystic Fibrosis Foundation supports (adult and pediatric) physicians who have completed at least two years of fellowship training in a subspecialty
Clinical Fellowship – 5th year (cystic fibrosis USA)
The 5th year Clinical Fellowship from the Cystic Fibrosis Foundation supports (adult and pediatric) physicians who have completed at least 4 years of fellowship training in a subspecialty related to
Clinical Fellowship – 1st and 2nd year (cystic fibrosis USA)
The 1st and 2nd year Clinical Fellowship from the Cystic Fibrosis Foundation supports first and second year clinical fellows to pursue training in cystic fibrosis-relevant subspecialties. The Fellowship must be
Project Funding (UK Ataxia-Telangiectasia)
The Project Funding from the A-T Society supports researchers working in the UK on Ataxia-Telangiectasia (A-T). The funding provides full or partial cover for investigator-initiated research projects for 2 years
Project Grants (Birt-Hogg Dubé Syndrome worldwide)
The Project Grants from the Myrovlytis Trust provides funding for researchers worldwide working on hypothesis-driven research related to Birt-Hogg Dubé Syndrome and its related kidney disorders and osteosarcoma. Applicants may
Studentship or Fellowships (UK Ataxia-Telangiectasia)
The Studentship or Fellowships from the A-T Society supports PhD students and postdoctoral fellows working in the UK on Ataxia-Telangiectasia (A-T). Applicants must be able to demonstrate that their work
MDA Clinical Research Network Grants (muscular dystrophy worldwide)
The MDA Clinical Research Network Grants from the Muscular Dystrophy Association support clinical researchers worldwide working on muscular dystrophy. The grants support MDA researchers to form a network to promote and
Prader-Willi Research Grant (worldwide)
The Prader-Willi Research Grant from the Foundation for Prader-Willi Research (FPWR) provides funding for innovative, high-risk/high-reward research addressing Prader-Willi syndrome. Current funding priorities are given to: Applications are open to
MDA Clinical Research Grants (muscular dystrophy worldwide)
The MDA Clinical Research Grants from the Muscular Dystrophy Association support clinical researchers worldwide working on muscular dystrophy. Applicants must hold a Doctor of Medicine (M.D.), Doctor of Philosophy (Ph.D.),
Small/Pilot Studies (Birt-Hogg Dubé syndrome | worldwide)
The Pilot Studies grant from the Myrovlytis Trust provides funding for researchers worldwide working on hypothesis-generating research related to Birt-Hogg Dubé Syndrome and its related kidney disorders and osteosarcoma. Applicants
2023 AFTD Holloway Fellowships (frontotemporal degeneration worldwide)
The AFTD Holloway Fellowships from The Association for Frontotemporal Degeneration (AFTD) support postdoctoral researchers working on frontotemporal degeneration worldwide. Applicants must have completed a PhD or an MD and the
